(…continued from the previous post). There are several features that make the recent Adrenoleukodystrophy (ALD) gene transfer study noteworthy. 1- A New Viral Vector Debuts: this is the first successful application of HIV-derived viruses in gene transfer (lentiviruses). These vectors have various advantages over retroviruses used in other protocols. One is that, in theory, at… Continue reading More on Lenti’s, Gene Transfer and Adrenoleukodystrophy
Tag: ALD
Gene Transfer and Adrenoleukodystrophy: There Will Always Be Paris
Last week’s Science magazine reported what seems likely to count as one of gene transfer’s greatest clinical successes to date: stabilization of adrenoleukodystrophy in two boys receiving genetically modified blood stem cells. Preliminary results of this study had been presented at this summer’s American Society of Gene and Cell Therapy meeting. Adrenoleukodystrophy (ALD) is a… Continue reading Gene Transfer and Adrenoleukodystrophy: There Will Always Be Paris